Rare Disease
Emma Viscidi, PhD
Biogen
Cambridge, Massachusetts, United States
Nasha Wang
Biogen, United States
Li Li
Biogen, United States
Susan Eaton
Biogen, United States
Giorgia Coratti
Physiotherapist
Pediatric Neurology, UniversitĂ Cattolica del Sacro Cuore, Rome, Italy, Italy
Salma Samsuddin
SMA-REACH & UK (ISMAC) Trial Manager
Dubowitz Neuromuscular Centre, UCL Institute of Child Health & Great Ormond Street Hospital, London, United Kingdom
Mariacristina Scoto
Neuromuscular Consultant & Honorary Associate Professor
Dubowitz Neuromuscular Centre, UCL Great Ormond Street Institute of Child Health, London, UK, United Kingdom
Annemarie Rohwer
Research Physiotherapist
Dubowitz Neuromuscular Centre, UCL Great Ormond Street Institute of Child Health, London, UK, United Kingdom
Francesco Muntoni
Pediatric Neurologist
NIHR Great Ormond Street Hospital Biomedical Research Centre, London, United Kingdom, United Kingdom
Richard S Finkel
Professor of Pediatric Neurology
St. Jude Children's Research Hospital, Memphis, TN, USA, United States
Eugenio Mercuri
Professor of Pediatric Neurology
Pediatric Neurology, UniversitĂ Cattolica del Sacro Cuore, Rome, Italy, Italy
Sue Hall
Biogen, United States